Delivery

Regulatory Delivery

Regulatory delivery at PrimeRA covers the full arc of submission and procedural work, from the first CTA or IND through to Marketing Authorisation, executed by a team with direct experience across the most complex ATMP programmes approved in the UK, EU and US. For companies managing a global development strategy, PrimeRA aligns UK, EU and US regulatory activity from the outset, protecting timelines across jurisdictions and ensuring the programme builds toward its commercial goals without costly rework. Our Delivery pillar works in close coordination with our Leadership pillar, which provides the strategic direction that guides execution.

What We Deliver

Regulatory execution across the full development arc

Delivery at PrimeRA covers the full range of regulatory execution - preparing, writing, reviewing and leading all procedures from initial pre-submission meeting packages through to Marketing Authorisation dossiers. The team integrates with the client's scientists and internal contributors at the depth the programme requires, filling resource gaps at any scale, and keeping key deliverables on track.

Two services form the structural backbone of how PrimeRA plans and manages delivery. The bespoke regulatory roadmap is a working planning document that places every regulatory milestone - submissions, agency meetings, designations - in the context of data generation timelines, giving leadership and investors a transparent view of dependencies, critical path decisions and what each milestone requires. The Regulatory Advisory Board service allows PrimeRA to contribute to or lead the formation of a client's RAB - hand-selecting consultants with the relevant modality and discipline expertise, preparing materials that frame questions with precision, and consolidating outputs into guidance that integrates directly into programme planning.

Clinical Stage
IND · CTA · IMPD

From first submission to first-in-human

PrimeRA prepares and leads the regulatory procedures required to move a programme into clinical development. This includes drafting and compiling IND and CTA applications, authoring the IMPD and Module 3, and building the meeting packages that establish the programme's regulatory position with the agency before a submission is filed. The team manages all agency interactions, ensuring positions are precisely framed, questions are anticipated and responses are coordinated without delay.

Accelerated pathway applications are a core component of clinical stage delivery. Orphan Designation (EU and US), PRIME, ILAP, Fast Track, Breakthrough Therapy, RMAT and RPDD each require tailored applications that draw on the clinical and scientific evidence package in ways that align precisely with the specific designation criteria. PrimeRA prepares these applications, advises on sequencing and timing to maximise the benefits obtained, and manages the agency interactions that follow.

IND and CTA preparation and submission
IMPD and Module 3 authoring and compilation
Agency meeting packages - INTERACT, Innovation Office, Type A, B, C and D FDA meetings; EMA Scientific Advice and Protocol Assistance; EU national scientific advice procedures
Orphan, PRIME, ILAP (MHRA), Fast Track, Breakthrough, RMAT and RPDD (FDA) designation applications
EMA and MHRA agency engagement and meeting management
FDA meeting strategy, preparation and follow-through (Type A, B, C and D)
Late Stage
MAA · BLA · PIP

End-to-end delivery through to authorisation

Marketing Authorisation is the most demanding regulatory procedure in drug development. The quality of the dossier, the coherence of the regulatory position and the management of the agency relationship all carry the greatest weight at this stage. PrimeRA takes full ownership of MAA and BLA delivery: authoring and reviewing all dossier sections, coordinating the submission procedure, managing Rapporteur and agency engagement throughout the evaluation, and preparing responses to questions across regulatory, CMC, non-clinical and clinical disciplines.

A Paediatric Investigational Plan is a mandatory regulatory requirement under EMA regulation, and paediatric strategy - including timing and the scope of the paediatric programme - is a consideration that should be resolved well before the MAA stage. PrimeRA prepares PIPs and manages the EMA negotiation process. For programmes with a US development path, PrimeRA also prepares the FDA Pediatric Study Plan (iPSP) — the US equivalent of the PIP. The bespoke regulatory roadmap is available at this stage, placing MAA filing, Rapporteur timelines and post-authorisation milestones in the context of data generation and the commercial decisions that depend on them.

MAA and BLA authoring, review and dossier management
Rapporteur and agency engagement and negotiation
Response preparation across regulatory, CMC, non-clinical and clinical disciplines
Paediatric Investigational Plan (PIP) preparation and EMA negotiation
FDA Pediatric Study Plan (iPSP) preparation
Accelerated pathway strategy - PRIME, ILAP, Breakthrough, Conditional MA
Bespoke regulatory roadmap preparation
Why PrimeRA

A track record built on programmes that changed the field

01
Proven at the frontier of ATMP development

Our team have contributed to the development, commercialisation and maintenance of numerous approved ATMPs including CAR-Ts, AAV, CRISPR and HSPC derived products.

02
Depth across modalities and platforms

PrimeRA has worked across AAV, Adenovirus and Lentivirus vectors; T-cell, HSPC and iPSC cell types; and gene editing techniques including CRISPR and Base Editing. This modality depth informs how PrimeRA evaluates regulatory pathways - including platform approaches and cross-modality strategies - to identify the most efficient route to approval for each programme.

03
Tailored to the programme

Every engagement is structured around what the programme needs - integrating with the client's scientific team at the depth the programme needs, stepping in at any point in the development arc, and scaling resource as milestones approach. The aim is consistent: protecting timelines and keeping deliverables on track.

What Is In Scope

From first submission to authorisation

Delivery covers the preparation, authoring and procedural execution of regulatory documents and submissions across the full development arc - from IND and CTA through to MAA and BLA, including designations, agency meetings and response work. Strategic direction and senior regulatory oversight sit under the Leadership pillar, which shapes the position and approach that Delivery executes.

✓ In scope
IND, CTA and IMPD preparation, authoring and submission
MAA and BLA authoring, dossier management and procedure coordination
Agency meeting packages - INTERACT, Innovation Office, Type A/B/C/D FDA meetings; EMA Scientific Advice and Protocol Assistance; EU national scientific advice
Orphan designation preparation and maintenance (EMA and FDA)
PRIME, ILAP, Fast Track, Breakthrough, RMAT, RPDD and Conditional MA applications
Paediatric Investigational Plan (PIP) preparation and negotiation
FDA Pediatric Study Plan (iPSP) preparation
Bespoke regulatory roadmap preparation
Response preparation across regulatory, CMC, non-clinical and clinical disciplines
Regulatory Advisory Board formation and coordination
→ Scoped separately
Senior regulatory leadership and strategic direction - see Leadership
Head of Regulatory or fractional leadership function - see Leadership
Regulatory representation with FDA, EMA and MHRA - see Representation
Investment due diligence and technology spin-out advisory - see Strategy & Insight
Standalone strategic advice without delivery context - see Strategy & Insight
FAQs

Common questions

PrimeRA has deep experience in advanced therapy medicinal products - including AAV and other viral vector gene therapies, CAR-T and other cell therapy products, and programmes using CRISPR and other gene editing techniques. The team has contributed to authorised ATMPs in both the EU and US, including several landmark programmes. We also work on rare disease products, paediatric medicines and complex biologics across a range of modalities.
Both. PrimeRA can take full ownership of a submission - authoring, compiling and managing the regulatory procedure end to end - or can work alongside internal or external contributors to fill specific resource gaps. The approach is always tailored to what the programme needs and what resource the client already has in place.
The two pillars are designed to work together. Leadership provides the senior strategic direction - shaping the regulatory position, overseeing the approach, and ensuring that what gets written is consistent with the agreed strategy. Delivery executes that strategy: authoring documents, managing submissions and coordinating with agencies. Where a client engages both, the result is a fully joined-up regulatory function.
Yes. At PrimeRA's we have worked with companies approaching their first CTA or IND. We are experienced in guiding teams through the full process for the first time - from regulatory roadmap and meeting preparation through to submission and agency response - and in calibrating the level of involvement to suit the team's own capability and capacity.
Yes. Meeting preparation - including pre-CTA/IND briefing documents, INTERACT packages and Innovation Office submissions - is a core part of the Delivery service. PrimeRA prepares the relevant documents, frames the programme's positions precisely for the agency, and supports the meeting itself including post-meeting responses and follow-through on any action items. Effective agency meeting strategy is one of the most consequential inputs to a development programme - how the programme is positioned before a meeting often determines the quality of the feedback received.
Yes. One of the structural advantages of working with PrimeRA is the ability to scale resource as programmes accelerate or milestones approach. This allows clients to maintain a lean and cost-effective regulatory structure in steady-state periods while having the depth to absorb high-activity phases without losing momentum, compromising quality or delaying submissions. For companies managing investor timelines and development milestones simultaneously, this flexibility is a direct protection against schedule risk.

PrimeRA · Delivery

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